From shaping care guidelines in the Netherlands to tackling gene therapy challenges at the MDA Summit, Cure CMD is driving progress in research and care. Join us at the 2025 SciFam Conference this August in Philadelphia—registration is open!

CMD Community Member, Justin Moy, shares his journey with LAMA2-related muscular dystrophy and his life quest to cure his own condition.

Modalis Therapeutics program for LAMA2-RD gene therapy granted Rare Pediatric Disease Designation by FDA.

We are honored to support groundbreaking discoveries related to LMNA-CMD.

We are thrilled to announce a new clinical workshop focused on establishing CMD subtype-specific care recommendations.

We are honored to support groundbreaking discoveries related to Dystroglycanopathy.

We are honored to support groundbreaking discoveries related to LAMA2-Related Dystrophy.

The MAGIC research team welcomes iMM to the consortium to add a cellular perspective to muscle-on-chip technologies

Long-awaited publication about the Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy now published.

We are honored to support groundbreaking discoveries related to SELENON-Related Disorders.

Explore an in-depth interview with Gustavo Dziewczapolski, Doctor in Neuropharmacology and Scientific Director of Cure CMD. Gain insights in

Cure CMD’s Scientific Director, Dr. Gustavo Dziewczapolski, provides a recap of his attendance at the 8th International Myology Congress in

We are honored to support groundbreaking discoveries in Collagen 6-Related Dystrophies (COL6-RD).

Expanding on nearly a decade of partnership in the life sciences, the Translational Sciences team at UPMC Enterprises and the University...

This year, the MDBR's Team Cure CMD raised $140k for research.

Prof. Jeanette Erdmann, CMD Researcher and CMD-affected individual passed away unexpectedly after a tragic fall.

$482,000 Awarded for CMD Science We are thrilled to announce the newest round of research grants focused on congenital muscular...

On the road toward treatments and a cure for congenital muscular dystrophy, we’ve come a long, long way to learn about causes and...

Thanks to everyone who participated in our 2021 Virtual SciFam Conference. If you didn't get a chance to attend or watch recordings in...

Congratulations CMD Researcher and Community Member, Dr. Jeannette Erdmann! We are thrilled to share that CMD researcher and...