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2019 SciFam Lay Summary: Stronger Together

A “Triad” of patient advocacy organizations for ultra-rare congenital muscular diseases, Cure CMD (Congenital Muscular Dystrophy), A...

Meet Veronica Pini: Researcher, Community Member

“I’m a very curious person,” says Veronica Pini, PhD student who stands just under five feet tall with long blond hair. Her...

Cure CMD Co-Funds SEPN1 Research Project with AFM

Cure CMD (Congenital Muscular Dystrophy) is eager to announce a co-funded grant, in partnership with AFM-Téléthon, for Dr. Esther Zito’s...

Cure CMD Co-Funds LMNA Research Grant with Muscular Dystrophy UK

Cure CMD (Congenital Muscular Dystrophy) is pleased to announce the recipient of a grant co-funded with Muscular Dystrophy UK: Dr. Giséle...

2018 Team Cure CMD - Million Dollar Bike Ride Raises $100k for Collagen VI Research

Cure CMD has great news! Earlier this year, we shared about the Million Dollar Bike Ride, an annual event held at PENN Orphan Disease...

Research Grant Award for Collagen VI

Cure CMD is thrilled to announce the 2018-2019 International Research Grant Award for Collagen VI-CMD! Dr. Stefano Squarzoni: two years...

Two Research Grant Awards for LAMA2

Cure CMD is thrilled to announce the 2018-2019 International Research Grant Awards for LAMA2-CMD! Research projects focused on LAMA2 have...

Research Grant Award for SEPN1

Cure CMD is thrilled to announce the 2018-2019 International Research Grant Award for SEPN1-RM! Dr. Ana Ferreiro: two years of funding...

Gene Correction Therapy Study, Seed-Funded by Cure CMD, Continues through MDA Grant

What: A $180,000 grant has just been announced by the Muscular Dystrophy Association (MDA) to fund the exploration of potential of gene...

Santhera Announces Successful Completion of First Clinical Trial with Omigapil in Patients with Cong

Please see the end of this article for Frequently Asked Questions - CALLISTO Phase 1 Clinical Trial Pratteln, Switzerland, April 5, 2018...